In October 2023, the Yaya Foundation hosted its 2023 Family & Scientific Conference, which brought together more than 100 families, researchers, and clinicians in our 4H Leukodystrophy Community.
In this presentation, Dr. Jun Xie of the University of Massachusetts (UMass) Chan Medical School gives an overview of gene therapy and how it can be potentially used to treat conditions like 4H Leukodystrophy.
In everything we do, we’re working to speed progress toward a cure. Learn more about our ambitious research strategy.
Learn More >>We are driven by the dream that one day, every child with 4H Leukodystrophy will have the chance to live a long, healthy life.
So we fight for these children by acting as a catalyst and a connector—bringing researchers together to accelerate the pace of discovery, while connecting families with vital education resources and emotional support.
We won’t stop until we find a treatment and, ultimately, a cure.
Your generous donation funds critical research into life-changing treatments and a cure for 4H Leukodystrophy, as well as vital programs that connect, support and empower families affected by this rare disease. All it takes is a simple click.
